% IMPORTANT: The following is UTF-8 encoded. This means that in the presence
% of non-ASCII characters, it will not work with BibTeX 0.99 or older.
% Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or
% “biber”.
@ARTICLE{Fitzgerald:139474,
author = {Fitzgerald, Julia and Zimprich, Alexander and Carvajal
Berrio, Daniel A and Schindler, Kevin M and Maurer, Brigitte
and Schulte, Claudia and Bus, Christine and Hauser,
Ann-Kathrin and Kübler, Manuela and Lewin, Rahel and
Bobbili, Dheeraj Reddy and Schwarz, Lisa M and
Vartholomaiou, Evangelia and Brockmann, Kathrin and Wüst,
Richard and Madlung, Johannes and Nordheim, Alfred and
Riess, Olaf and Martins, L Miguel and Glaab, Enrico and May,
Patrick and Schenke-Layland, Katja and Picard, Didier and
Sharma, Manu and Gasser, Thomas and Krüger, Rejko},
title = {{M}etformin reverses {TRAP}1 mutation-associated
alterations in mitochondrial function in {P}arkinson's
disease.},
journal = {Brain},
volume = {140},
number = {9},
issn = {0006-8950},
address = {Oxford},
publisher = {Oxford Univ. Press},
reportid = {DZNE-2020-05796},
pages = {2444-2459},
year = {2017},
abstract = {The mitochondrial proteins TRAP1 and HTRA2 have previously
been shown to be phosphorylated in the presence of the
Parkinson's disease kinase PINK1 but the downstream
signalling is unknown. HTRA2 and PINK1 loss of function
causes parkinsonism in humans and animals. Here, we
identified TRAP1 as an interactor of HTRA2 using an unbiased
mass spectrometry approach. In our human cell models, TRAP1
overexpression is protective, rescuing HTRA2 and
PINK1-associated mitochondrial dysfunction and suggesting
that TRAP1 acts downstream of HTRA2 and PINK1. HTRA2
regulates TRAP1 protein levels, but TRAP1 is not a direct
target of HTRA2 protease activity. Following genetic
screening of Parkinson's disease patients and healthy
controls, we also report the first TRAP1 mutation leading to
complete loss of functional protein in a patient with late
onset Parkinson's disease. Analysis of fibroblasts derived
from the patient reveal that oxygen consumption, ATP output
and reactive oxygen species are increased compared to
healthy individuals. This is coupled with an increased pool
of free NADH, increased mitochondrial biogenesis, triggering
of the mitochondrial unfolded protein response, loss of
mitochondrial membrane potential and sensitivity to
mitochondrial removal and apoptosis. These data highlight
the role of TRAP1 in the regulation of energy metabolism and
mitochondrial quality control. Interestingly, the diabetes
drug metformin reverses mutation-associated alterations on
energy metabolism, mitochondrial biogenesis and restores
mitochondrial membrane potential. In summary, our data show
that TRAP1 acts downstream of PINK1 and HTRA2 for
mitochondrial fine tuning, whereas TRAP1 loss of function
leads to reduced control of energy metabolism, ultimately
impacting mitochondrial membrane potential. These findings
offer new insight into mitochondrial pathologies in
Parkinson's disease and provide new prospects for targeted
therapies.},
keywords = {Adenosine Triphosphate: metabolism / Apoptosis: drug
effects / Case-Control Studies / Cells, Cultured /
Fibroblasts: metabolism / HSP90 Heat-Shock Proteins:
biosynthesis / HSP90 Heat-Shock Proteins: genetics /
High-Temperature Requirement A Serine Peptidase 2 / Humans /
Membrane Potential, Mitochondrial: physiology / Metformin:
therapeutic use / Mitochondria: drug effects / Mitochondria:
genetics / Mitochondria: metabolism / Mitochondrial
Proteins: metabolism / Mutation / NAD: metabolism /
Organelle Biogenesis / Oxygen Consumption / Parkinson
Disease: drug therapy / Parkinson Disease: genetics /
Parkinson Disease: metabolism / Protein Kinases: metabolism
/ Reactive Oxygen Species: metabolism / Serine
Endopeptidases: metabolism / HSP90 Heat-Shock Proteins (NLM
Chemicals) / Mitochondrial Proteins (NLM Chemicals) /
Reactive Oxygen Species (NLM Chemicals) / TRAP1 protein,
human (NLM Chemicals) / NAD (NLM Chemicals) / Adenosine
Triphosphate (NLM Chemicals) / Metformin (NLM Chemicals) /
Protein Kinases (NLM Chemicals) / PTEN-induced putative
kinase (NLM Chemicals) / Serine Endopeptidases (NLM
Chemicals) / HTRA2 protein, human (NLM Chemicals) /
High-Temperature Requirement A Serine Peptidase 2 (NLM
Chemicals)},
cin = {AG Gasser / AG Berg ; AG Berg / Ext HIH / Ext UKT /
Tübingen common},
ddc = {610},
cid = {I:(DE-2719)1210000 / I:(DE-2719)5000055 /
I:(DE-2719)5000057 / I:(DE-2719)5000058 /
I:(DE-2719)6000018},
pnm = {345 - Population Studies and Genetics (POF3-345)},
pid = {G:(DE-HGF)POF3-345},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:29050400},
doi = {10.1093/brain/awx202},
url = {https://pub.dzne.de/record/139474},
}