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@ARTICLE{Llonch:139746,
author = {Llonch, Sílvia and Carido, Magdalena and Ader, Marius},
title = {{O}rganoid technology for retinal repair.},
journal = {Developmental biology},
volume = {433},
number = {2},
issn = {0012-1606},
address = {Amsterdam [u.a.]},
publisher = {Elsevier},
reportid = {DZNE-2020-06068},
pages = {132-143},
year = {2018},
abstract = {A major cause for vision impairment and blindness in
industrialized countries is the loss of the light-sensing
retinal tissue in the eye. Photoreceptor damage is one of
the main characteristics found in retinal degeneration
diseases, such as Retinitis Pigmentosa or age-related
macular degeneration. The lack of effective therapies to
stop photoreceptor loss together with the absence of
significant intrinsic regeneration in the human retina
converts such degenerative diseases into permanent
conditions that are currently irreversible. Cell replacement
by means of photoreceptor transplantation has been proposed
as a potential approach to tackle cell loss in the retina.
Since the first attempt of photoreceptor transplantation in
humans, about twenty years ago, several research groups have
focused in the development and improvement of technologies
necessary to bring cell transplantation for retinal
degeneration diseases to reality. Progress in recent years
in the generation of human tissue derived from pluripotent
stem cells (PSCs) has significantly improved our tools to
study human development and disease in the dish.
Particularly the availability of 3D culture systems for the
generation of PSC-derived organoids, including the human
retina, has dramatically increased access to human material
for basic and medical research. In this review, we focus on
important milestones towards the generation of
transplantable photoreceptor precursors from PSC-derived
retinal organoids and discuss recent pre-clinical
transplantation studies using organoid-derived
photoreceptors in context to related in vivo work using
primary photoreceptors as donor material. Additionally, we
summarize remaining challenges for developing photoreceptor
transplantation towards clinical application.},
subtyp = {Review Article},
keywords = {Translational Research, Biomedical / Animals / Cellular
Reprogramming Techniques / Culture Media, Serum-Free:
pharmacology / Embryonic Stem Cells: cytology / Embryonic
Stem Cells: drug effects / Humans / Induced Pluripotent Stem
Cells: transplantation / Mice / Morphogenesis / Organoids:
transplantation / Photoreceptor Cells, Vertebrate:
transplantation / Pluripotent Stem Cells: transplantation /
Retina: cytology / Retinal Degeneration: therapy / Species
Specificity / Tissue Culture Techniques / Translational
Medical Research / Culture Media, Serum-Free (NLM
Chemicals)},
cin = {AG Karl},
ddc = {570},
cid = {I:(DE-2719)1710004},
pnm = {342 - Disease Mechanisms and Model Systems (POF3-342)},
pid = {G:(DE-HGF)POF3-342},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:29291970},
doi = {10.1016/j.ydbio.2017.09.028},
url = {https://pub.dzne.de/record/139746},
}