TY - JOUR AU - Ackermann, Frauke AU - Schink, Kay Oliver AU - Bruns, Christine AU - Izsvák, Zsuzsanna AU - Hamra, F Kent AU - Rosenmund, Christian AU - Garner, Craig Curtis TI - Critical role for Piccolo in synaptic vesicle retrieval. JO - eLife VL - 8 SN - 2050-084X CY - Cambridge PB - eLife Sciences Publications M1 - DZNE-2020-07042 SP - e46629 PY - 2019 AB - Loss of function of the active zone protein Piccolo has recently been linked to a disease, Pontocerebellar Hypoplasia type 3, which causes brain atrophy. Here, we address how Piccolo inactivation in rat neurons adversely affects synaptic function and thus may contribute to neuronal loss. Our analysis shows that Piccolo is critical for the recycling and maintenance of synaptic vesicles. We find that boutons lacking Piccolo have deficits in the Rab5/EEA1 dependent formation of early endosomes and thus the recycling of SVs. Mechanistically, impaired Rab5 function was caused by reduced synaptic recruitment of Pra1, known to interact selectively with the zinc finger domains of Piccolo. Importantly, over-expression of GTPase deficient Rab5 or the Znf1 domain of Piccolo restores the size and recycling of SV pools. These data provide a molecular link between the active zone and endosome sorting at synapses providing hints to how Piccolo contributes to developmental and psychiatric disorders. KW - Animals KW - Axons: metabolism KW - Cytoskeletal Proteins: metabolism KW - DNA Transposable Elements: genetics KW - Endosomes: metabolism KW - GTP Phosphohydrolases: metabolism KW - Gene Knockout Techniques KW - Guanosine Diphosphate: metabolism KW - Models, Biological KW - Mutagenesis: genetics KW - Neuropeptides: metabolism KW - Phosphatidylinositol Phosphates: metabolism KW - Rats KW - Synaptic Vesicles: metabolism KW - Synaptic Vesicles: ultrastructure KW - Synaptophysin: metabolism KW - Vesicular Transport Proteins: metabolism KW - rab5 GTP-Binding Proteins: metabolism LB - PUB:(DE-HGF)16 C6 - pmid:31074746 C2 - pmc:PMC6541439 DO - DOI:10.7554/eLife.46629 UR - https://pub.dzne.de/record/140720 ER -