% IMPORTANT: The following is UTF-8 encoded. This means that in the presence
% of non-ASCII characters, it will not work with BibTeX 0.99 or older.
% Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or
% “biber”.
@INPROCEEDINGS{LlorensTorres:150981,
author = {Llorens Torres, Francesc Josep and Thüne, Katrin and
Gotzmann, Nadine and Cramm, Maria},
title = {{I}dentification of new molecular alterations in {F}atal
{F}amilial {I}nsomnia},
journal = {Prion},
volume = {10},
number = {sup1},
issn = {1933-6896},
reportid = {DZNE-2020-01040},
pages = {S37-S127},
year = {2016},
abstract = {Fatal familial insomnia (FFI) is an autosomaldominant prion
disease caused by a D178Nmutation in PRNP in combination
with methio-nine at codon 129 in the mutated allele of
thesame gene. The present study analyzes patho-logical and
molecular features in 7 FFI casescarrying the mutation D178N
and M homozy-gous at the codon 129 of PRNP. Severe neuro-nal
loss and marked astrocytic gliosis wasobserved in every case
in the mediodorsal andanterior nuclei of the thalamus
whereas theentorhinal cortex (EC) was variably affected.
Spongiform degeneration was only observed inthe EC. Synaptic
and fine granular PrPScimmu-noreactivity was found in
theECbut not in thal-amus. Microglia was barely increased in
themediodorsal thalamus, but mRNA expressionof IL6, IL10RA,
CSF3R and TLR7 was foundin the thalamus in FFI. PrPClevels
were signifi-cantly decreased in the thalamus,ECand
cere-bellum in FFI compared with controls.However, increased
expression of the non-gly-cosylated band of about 19 kDa was
observedin the thalamus when using PrP antibodiesmapping to
the central region of the PrP com-prising thea-helix domains
H1 and H2.Decreased PrP mRNA levels were alsoobserved in the
thalamus andEC. Altered PrPsolubility was observed in FFI
compared withcontrols; significantly reduced PrP levels in
thecytoplasmic fraction and increased insolublelevels were
found in FFI cases when comparedwith controls. Amyloid-like
deposits were onlyseen in theEC. RT-QuIC assay which
mimicsinvitrothe conversion of PrPc to misfolded andamyloid
PrP revealed that all the FFI samplesof the entorhinal
cortex were positive whereasthe thalamus was positive only
in 3 cases; thecerebellum was positive in 2 cases. All
controlswere negative. The expression of subunits
ofmitochondrial respiratory complexes and com-ponents of the
protein synthesis machineryfrom the nucleolus to the
ribosome was ana-lyzed in the mediodorsal thalamus.
NDUFB8(complex I subunit), SDHB (complex II sub-unit),
UQCRC2 (complex III subunit), COX2(complex IV subunit) and
ATP50 (complex Vsubunit) expression levels were reduced in
FFI.Voltage-dependent anion channel and ATP5Hwere also
reduced. In contrast, a markedincrease in superoxide
dismutase 2 was foundin reactive astrocytes. The
histone-bindingchaperones nucleolin and nucleoplasmin 3,
andhistone H3 di-methylated K9 were markedlyreduced together
with a decrease in the expres-sion of protein transcription
elongation factoreEF1A in mediodorsal thalamus.},
month = {May},
date = {2016-05-10},
organization = {PRION 2016, Tokyo (Japan), 10 May 2016
- 13 May 2016},
cin = {AG Zerr},
ddc = {570},
cid = {I:(DE-2719)1440011-1},
pnm = {344 - Clinical and Health Care Research (POF3-344)},
pid = {G:(DE-HGF)POF3-344},
typ = {PUB:(DE-HGF)1 / PUB:(DE-HGF)16},
pubmed = {pmid:27088811},
doi = {10.1080/19336896.2016.1162644},
url = {https://pub.dzne.de/record/150981},
}