% IMPORTANT: The following is UTF-8 encoded. This means that in the presence
% of non-ASCII characters, it will not work with BibTeX 0.99 or older.
% Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or
% “biber”.
@ARTICLE{Tavares:153442,
author = {Tavares, Tamara Paulo and Mitchell, Derek G V and Coleman,
Kristy KL and Coleman, Brenda L and Shoesmith, Christen L
and Butler, Christopher R and Santana, Isabel and Danek,
Adrian and Gerhard, Alexander and de Mendonca, Alexandre and
Borroni, Barbara and Tartaglia, Maria Carmela and Graff,
Caroline and Galimberti, Daniela and Tagliavini, Fabrizio
and Moreno, Fermin and Frisoni, Giovanni and Rowe, James
Benedict and Levin, Johannes and Van Swieten, John Cornelis
and Otto, Markus and Synofzik, Matthis and Sanchez-Valle,
Raquel and Vandenberghe, Rik and Laforce, Robert Jr and
Ghidoni, Roberta and Sorbi, Sandro and Ducharme, Simon and
Masellis, Mario and Rohrer, Jonathan and Finger, Elizabeth},
title = {{E}arly symptoms in symptomatic and preclinical genetic
frontotemporal lobar degeneration},
journal = {Journal of neurology, neurosurgery, and psychiatry},
volume = {91},
number = {9},
issn = {1468-330X},
address = {London},
publisher = {BMJ Publishing Group},
reportid = {DZNE-2020-01439},
pages = {975 - 984},
year = {2020},
abstract = {Objectives The clinical heterogeneity of frontotemporal
dementia (FTD) complicates identification of biomarkers for
clinical trials that may be sensitive during the
prediagnostic stage. It is not known whether cognitive or
behavioural changes during the preclinical period are
predictive of genetic status or conversion to clinical FTD.
The first objective was to evaluate the most frequent
initial symptoms in patients with genetic FTD. The second
objective was to evaluate whether preclinical mutation
carriers demonstrate unique FTD-related symptoms relative to
familial mutation non-carriers.Methods The current study
used data from the Genetic Frontotemporal Dementia
Initiative multicentre cohort study collected between 2012
and 2018. Participants included symptomatic carriers (n=185)
of a pathogenic mutation in chromosome 9 open reading frame
72 (C9orf72), progranulin (GRN) or microtubule-associated
protein tau (MAPT) and their first-degree biological family
members (n=588). Symptom endorsement was documented using
informant and clinician-rated scales.Results The most
frequently endorsed initial symptoms among symptomatic
patients were apathy $(23\%),$ disinhibition $(18\%),$
memory impairments $(12\%),$ decreased fluency $(8\%)$ and
impaired articulation $(5\%).$ Predominant first symptoms
were usually discordant between family members. Relative to
biologically related non-carriers, preclinical MAPT carriers
endorsed worse mood and sleep symptoms, and C9orf72 carriers
endorsed marginally greater abnormal behaviours. Preclinical
GRN carriers endorsed less mood symptoms compared with
non-carriers, and worse everyday skills.Conclusion
Preclinical mutation carriers exhibited neuropsychiatric
symptoms compared with non-carriers that may be considered
as future clinical trial outcomes. Given the heterogeneity
in symptoms, the detection of clinical transition to
symptomatic FTD may be best captured by composite indices
integrating the most common initial symptoms for each
genetic group},
keywords = {Adult / C9orf72 Protein: genetics / Female / Frontotemporal
Dementia: diagnosis / Frontotemporal Dementia: genetics /
Heterozygote / Humans / Male / Middle Aged / Mutation /
Prodromal Symptoms / Progranulins: genetics / tau Proteins:
genetics},
cin = {U Clinical Researchers - München / AG Gasser 1 / AG
Höglinger 2 / Clinical Dementia Research München},
ddc = {610},
cid = {I:(DE-2719)7000003 / I:(DE-2719)1210000 /
I:(DE-2719)1111015 / I:(DE-2719)1111016},
pnm = {344 - Clinical and Health Care Research (POF3-344) / 345 -
Population Studies and Genetics (POF3-345)},
pid = {G:(DE-HGF)POF3-344 / G:(DE-HGF)POF3-345},
typ = {PUB:(DE-HGF)16},
pmc = {pmc:PMC7611534},
pubmed = {pmid:32769115},
doi = {10.1136/jnnp-2020-322987},
url = {https://pub.dzne.de/record/153442},
}