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@ARTICLE{Malhis:162730,
author = {Malhis, Marwa and Kaniyappan, Senthilvelrajan and Aillaud,
Isabelle and Chandupatla, Ram Reddy and Ramirez, Lisa-Marie
and Zweckstetter, Markus and Horn, Anselm H C and Mandelkow,
Eckhard and Sticht, Heinrich and Funke, Susanne Aileen},
title = {{P}otent {T}au {A}ggregation {I}nhibitor {D}-{P}eptides
{S}elected against {T}au-{R}epeat 2 {U}sing {M}irror {I}mage
{P}hage {D}isplay.},
journal = {ChemBioChem},
volume = {22},
number = {21},
issn = {1439-7633},
address = {Weinheim},
publisher = {Wiley-VCH},
reportid = {DZNE-2021-01387},
pages = {3049 - 3059},
year = {2021},
abstract = {Alzheimer's disease and other Tauopathies are associated
with neurofibrillary tangles composed of Tau protein, as
well as toxic Tau oligomers. Therefore, inhibitors of
pathological Tau aggregation are potentially useful
candidates for future therapies targeting Tauopathies. Two
hexapeptides within Tau, designated PHF6* (275-VQIINK-280)
and PHF6 (306-VQIVYK-311), are known to promote Tau
aggregation. Recently, the PHF6* segment has been described
as the more potent driver of Tau aggregation. We therefore
employed mirror-image phage display with a large peptide
library to identify PHF6* fibril binding peptides consisting
of D-enantiomeric amino acids. The suitability of
D-enantiomeric peptides for in vivo applications, which are
protease stable and less immunogenic than L-peptides, has
already been demonstrated. The identified D-enantiomeric
peptide MMD3 and its retro-inverso form, designated MMD3rev,
inhibited in vitro fibrillization of the PHF6* peptide, the
repeat domain of Tau as well as full-length Tau. Dynamic
light scattering, pelleting assays and atomic force
microscopy demonstrated that MMD3 prevents the formation of
tau β-sheet-rich fibrils by diverting Tau into large
amorphous aggregates. NMR data suggest that the
D-enantiomeric peptides bound to Tau monomers with rather
low affinity, but ELISA (enzyme-linked immunosorbent assay)
data demonstrated binding to PHF6* and full length Tau
fibrils. In addition, molecular insight into the binding
mode of MMD3 to PHF6* fibrils were gained by in silico
modelling. The identified PHF6*-targeting peptides were able
to penetrate cells. The study establishes PHF6* fibril
binding peptides consisting of D-enantiomeric amino acids as
potential molecules for therapeutic and diagnostic
applications in AD research.},
keywords = {Humans / Peptide Library / Peptides: chemistry / Peptides:
pharmacology / Protein Aggregates: drug effects / tau
Proteins: antagonists $\&$ inhibitors / tau Proteins:
metabolism / Alzheimer's disease (Other) / D-peptides
(Other) / phage display (Other) / tau aggregation inhibitors
(Other) / therapy (Other)},
cin = {AG (Eva) Mandelkow / AG (Eckhard) Mandelkow / AG
Zweckstetter},
ddc = {540},
cid = {I:(DE-2719)1013015 / I:(DE-2719)1013014 /
I:(DE-2719)1410001},
pnm = {352 - Disease Mechanisms (POF4-352)},
pid = {G:(DE-HGF)POF4-352},
typ = {PUB:(DE-HGF)16},
pmc = {pmc:PMC8596876},
pubmed = {pmid:34375027},
doi = {10.1002/cbic.202100287},
url = {https://pub.dzne.de/record/162730},
}