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@ARTICLE{Wirth:282565,
author = {Wirth, Thomas and Faber, Jennifer and Depienne, Christel
and Roze, Emmanuel and Honnorat, Jérôme and Meissner,
Wassilios G and Giunti, Paola and Tranchant, Christine and
Klockgether, Thomas and Anheim, Mathieu},
title = {{P}rogress and challenges in sporadic late-onset cerebellar
ataxias.},
journal = {Nature reviews / Neurology},
volume = {21},
number = {12},
issn = {1759-4758},
address = {London},
publisher = {Macmillan Publishers Limited, part of Springer Nature},
reportid = {DZNE-2025-01328},
pages = {687 - 705},
year = {2025},
abstract = {Sporadic late-onset cerebellar ataxia (SLOCA) is a syndrome
defined by subacute or chronic and progressive ataxia
occurring after the age of 40 years in individuals without a
family history of ataxia. The 2022 publication of revised
consensus diagnostic criteria for multiple system atrophy
and the emergence of promising biomarkers provides a
thorough diagnostic framework that now enables the diagnosis
of numerous acquired causes of SLOCA, including autoimmune
disorders and neurodegenerative diseases. The ongoing
development and increased availability of DNA sequencing
technology have uncovered several molecular causes of SLOCA
besides spastic paraplegia type 7 and very late-onset
Friedreich ataxia. These additional causes include sporadic
genetic disorders, such as spinocerebellar atrophy type 27B,
caused by GAA expansion in the FGF14 gene, and cerebellar
ataxia with neuropathy and vestibular areflexia syndrome
(CANVAS), caused by biallelic expansions in the RFC1 gene.
This Review presents an updated clinical approach to the
diagnosis and management of SLOCA that focuses on the most
important developments in this field. Future challenges are
also discussed, including the identification of additional
missing genetic causes of SLOCA, especially via the use of
long-read genome sequencing, improvements in SLOCA
prognostication and the implementation of clinical trials of
neuroprotective interventions.},
subtyp = {Review Article},
keywords = {Humans / Cerebellar Ataxia: diagnosis / Cerebellar Ataxia:
genetics / Cerebellar Ataxia: therapy / Age of Onset},
cin = {Clinical Research (Bonn) / Patient Studies (Bonn)},
ddc = {610},
cid = {I:(DE-2719)1011001 / I:(DE-2719)1011101},
pnm = {353 - Clinical and Health Care Research (POF4-353)},
pid = {G:(DE-HGF)POF4-353},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:40983776},
doi = {10.1038/s41582-025-01136-0},
url = {https://pub.dzne.de/record/282565},
}