% IMPORTANT: The following is UTF-8 encoded. This means that in the presence
% of non-ASCII characters, it will not work with BibTeX 0.99 or older.
% Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or
% “biber”.
@ARTICLE{Gao:285035,
author = {Gao, Jincheng and Bader, Almke and Linder, Monika I and
Cheng, Jingyuan and Richter, Mathis and da Costa, Raul and
Zehrer, Annette and Mitt, Karl and Popper, Bastian and
Meissner, Felix and Wei, Xiang and de Vega Gómez, Enrique
and Tatematsu, Megumi and Rohlfs, Meino and Frenz-Wiessner,
Stephanie and Kiziltug, Mehmet and Somekh, Ido and
Yacobovich, Joanne and Steinberg-Shemer, Orna and Somech,
Raz and Soehnlein, Oliver and Schmid, Bettina and Klein,
Christoph and Walzog, Barbara and Maier-Begandt, Daniela},
title = {{M}utations in {VPS}18 lead to a neutrophil maturation
defect associated with disturbed vesicle homeostasis.},
journal = {Cell death $\&$ disease},
volume = {17},
number = {1},
issn = {2041-4889},
address = {London [u.a.]},
publisher = {Nature Publishing Group},
reportid = {DZNE-2026-00160},
pages = {180},
year = {2026},
abstract = {Neutrophils, the first cells to arrive at the site of
inflammation, are rather short-lived cells and thus have to
be constantly replenished. During neutrophil development,
vesicle dynamics need to be fine-tuned and impaired vesicle
trafficking has been linked to failure in neutrophil
maturation. Here, we characterized the role of VPS18 as a
central core component of CORVET $\&$ HOPS tethering
complexes for neutrophil development. Using
CRISPR/Cas9-engineered Hoxb8 cells with heterozygous
mutations in Vps18, we found that VPS18 deficiency
interfered with neutrophil development due to tethering
complex instability. As a result, vesicle dynamics were
impaired with a strong increase in LC3B-II and p62 levels,
indicating autophagosome accumulation and reduced autophagic
flux. With transmission electron microscopy, we verified the
increase in autophagosomes and also found irregularly shaped
vesicular structures in Vps18 mutants. Subsequently, Vps18
mutant neutrophil progenitors underwent premature apoptosis.
We described a novel patient with a heterozygous stop-gain
mutation in VPS18 suffering from neutropenia and recurrent
infections. To verify our findings in the human system, we
used human induced pluripotent stem cells (iPSCs). Upon
differentiation into neutrophils, loss of VPS18 resulted in
an almost complete absence of iPSC-derived developing
neutrophils. Heterozygous VPS18 mutant and patient
mutation-harboring iPSCs were characterized by strongly
reduced numbers of developing neutrophils. Zebrafish larvae
with heterozygous mutations in vps18 were also characterized
by significantly reduced neutrophil numbers. This study
shows the pivotal impact of VPS18 for adequate vesicle
dynamics during neutrophil development which might be
relevant in the context of vesicle trafficking during
granulopoiesis and congenital neutropenia.},
keywords = {Neutrophils: metabolism / Neutrophils: pathology / Animals
/ Humans / Vesicular Transport Proteins: genetics /
Vesicular Transport Proteins: metabolism / Zebrafish /
Mutation: genetics / Homeostasis / Cell Differentiation /
Induced Pluripotent Stem Cells: metabolism / Autophagy /
CRISPR-Cas Systems / Neutropenia: genetics / Neutropenia:
pathology / Autophagosomes: metabolism / Male / Vesicular
Transport Proteins (NLM Chemicals)},
cin = {AG Schmid München},
ddc = {570},
cid = {I:(DE-2719)1140002},
pnm = {352 - Disease Mechanisms (POF4-352)},
pid = {G:(DE-HGF)POF4-352},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:41526335},
doi = {10.1038/s41419-025-08338-w},
url = {https://pub.dzne.de/record/285035},
}