%0 Journal Article
%A Schoenmakers, Daphne H
%A Beerepoot, Shanice
%A Adang, Laura A
%A Asbreuk, Marije A B C
%A Bergner, Caroline G
%A Bley, Annette E
%A Boelens, Jaap-Jan
%A Calbi, Valeria
%A Darling, Alejandra
%A Eklund, Erik
%A García Cazorla, Ángeles
%A Grønborg, Sabine W
%A Groeschel, Samuel
%A van Hasselt, Peter M
%A Hollak, Carla E M
%A Horgan, Claire
%A Jones, Simon
%A de Koning, Tom
%A Laugwitz, Lucia
%A Lindemans, Caroline
%A Martin, Pascal
%A Mochel, Fanny
%A Øberg, Andreas
%A Ram, Dipak
%A Sevin, Caroline
%A Schöls, Ludger
%A Zerem, Ayelet
%A Wolf, Nicole I
%A Fumagalli, Francesca
%T Gene therapy in advanced metachromatic leukodystrophy: tempering expectations
%J Protein & cell
%V 16
%N 1
%@ 1674-800X
%C Beijing
%I Higher Education Press
%M DZNE-2025-00213
%P 12 - 15
%D 2025
%F PUB:(DE-HGF)16
%9 Journal Article
%R 10.1093/procel/pwae065
%U https://pub.dzne.de/record/276141