Journal Article

DZNE-2025-00213

http://join2-wiki.gsi.de/foswiki/pub/Main/Artwork/join2_logo100x88.png Gene therapy in advanced metachromatic leukodystrophy: tempering expectations

Schoenmakers, D. H. ; Beerepoot, S. ; Adang, L. A. ; Asbreuk, M. A. B. C. ; Bergner, C. G. ; Bley, A. E. ; Boelens, J.-J. ; Calbi, V. ; Darling, A. ; Eklund, E. ; García Cazorla, Á. ; Grønborg, S. W. ; Groeschel, S. ; van Hasselt, P. M. ; Hollak, C. E. M. ; Horgan, C. ; Jones, S. ; de Koning, T. ; Laugwitz, L. ; Lindemans, C. ; Martin, P. ; Mochel, F. ; Øberg, A. ; Ram, D. ; Sevin, C. ; Schöls, L.DZNE* ; Zerem, A. ; Wolf, N. I. ; Fumagalli, F.

2025
Higher Education Press Beijing

This record in other databases:  

Please use a persistent id in citations: doi:10.1093/procel/pwae065

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Contributing Institute(s):

1. Clinical Neurogenetics (AG Schöls)

Research Program(s):

1. 353 - Clinical and Health Care Research (POF4-353) (POF4-353)

Appears in the scientific report 2025

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Database coverage:
; ; ; ; Article Processing Charges ; BIOSIS Previews ; Biological Abstracts ; Clarivate Analytics Master Journal List ; DOAJ Seal ; Essential Science Indicators ; Fees ; IF >= 20 ; JCR ; SCOPUS ; Science Citation Index Expanded ; Web of Science Core Collection

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