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001 | 276141 | ||
005 | 20250209000705.0 | ||
024 | 7 | _ | |a 10.1093/procel/pwae065 |2 doi |
024 | 7 | _ | |a 1674-800X |2 ISSN |
024 | 7 | _ | |a 1674-8018 |2 ISSN |
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037 | _ | _ | |a DZNE-2025-00213 |
082 | _ | _ | |a 540 |
100 | 1 | _ | |a Schoenmakers, Daphne H |0 0000-0003-1601-7379 |b 0 |
245 | _ | _ | |a Gene therapy in advanced metachromatic leukodystrophy: tempering expectations |
260 | _ | _ | |a Beijing |c 2025 |b Higher Education Press |
336 | 7 | _ | |a article |2 DRIVER |
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700 | 1 | _ | |a Beerepoot, Shanice |0 0000-0003-2945-6784 |b 1 |
700 | 1 | _ | |a Adang, Laura A |0 0000-0002-8454-1116 |b 2 |
700 | 1 | _ | |a Asbreuk, Marije A B C |0 0009-0004-1709-6114 |b 3 |
700 | 1 | _ | |a Bergner, Caroline G |0 0000-0002-0327-1389 |b 4 |
700 | 1 | _ | |a Bley, Annette E |0 0000-0002-5514-0938 |b 5 |
700 | 1 | _ | |a Boelens, Jaap-Jan |0 0000-0003-2232-6952 |b 6 |
700 | 1 | _ | |a Calbi, Valeria |0 0000-0003-3514-666X |b 7 |
700 | 1 | _ | |a Darling, Alejandra |0 0000-0003-0344-5809 |b 8 |
700 | 1 | _ | |a Eklund, Erik |0 0000-0003-1902-4865 |b 9 |
700 | 1 | _ | |a García Cazorla, Ángeles |b 10 |
700 | 1 | _ | |a Grønborg, Sabine W |0 0000-0002-2113-9023 |b 11 |
700 | 1 | _ | |a Groeschel, Samuel |0 0000-0002-2706-7163 |b 12 |
700 | 1 | _ | |a van Hasselt, Peter M |0 0000-0001-9821-8398 |b 13 |
700 | 1 | _ | |a Hollak, Carla E M |0 0000-0003-0464-1078 |b 14 |
700 | 1 | _ | |a Horgan, Claire |0 0000-0002-6865-8509 |b 15 |
700 | 1 | _ | |a Jones, Simon |0 0000-0002-5117-0566 |b 16 |
700 | 1 | _ | |a de Koning, Tom |b 17 |
700 | 1 | _ | |a Laugwitz, Lucia |0 0000-0003-2506-1961 |b 18 |
700 | 1 | _ | |a Lindemans, Caroline |0 0000-0002-3984-5620 |b 19 |
700 | 1 | _ | |a Martin, Pascal |b 20 |
700 | 1 | _ | |a Mochel, Fanny |0 0000-0003-3970-3486 |b 21 |
700 | 1 | _ | |a Øberg, Andreas |0 0009-0000-9672-8247 |b 22 |
700 | 1 | _ | |a Ram, Dipak |b 23 |
700 | 1 | _ | |a Sevin, Caroline |0 0000-0002-5856-068X |b 24 |
700 | 1 | _ | |a Schöls, Ludger |0 P:(DE-2719)2810795 |b 25 |
700 | 1 | _ | |a Zerem, Ayelet |0 0000-0002-7923-4613 |b 26 |
700 | 1 | _ | |a Wolf, Nicole I |0 0000-0003-1721-0728 |b 27 |
700 | 1 | _ | |a Fumagalli, Francesca |0 0000-0001-7476-4087 |b 28 |
773 | _ | _ | |a 10.1093/procel/pwae065 |g Vol. 16, no. 1, p. 12 - 15 |0 PERI:(DE-600)2543451-2 |n 1 |p 12 - 15 |t Protein & cell |v 16 |y 2025 |x 1674-800X |
856 | 4 | _ | |y OpenAccess |u https://pub.dzne.de/record/276141/files/DZNE-2025-00213.pdf |
856 | 4 | _ | |y OpenAccess |x pdfa |u https://pub.dzne.de/record/276141/files/DZNE-2025-00213.pdf?subformat=pdfa |
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